Project: In Vivo Somatic Human Genome Editing for Genetic Diseases: Translating Novel Genome Editing and Engineered Delivery Vectors into Clinical Trials

This project is dedicated to developing a revolutionary genome editing medicine, taking a “DNA surgery” approach to fundamentally fix defective genes.
Precision genome editing, or “DNA surgery”, is a promising strategy to eliminate the root causes of diseases. Unlike traditional treatments that require long-term or even lifelong medication – often with diminishing effects over the later stage of every treatment cycle and risks recurrence, their approach aims to provide one-and-done solutions. Professor Zheng’s team is developing DNA surgery technology for programmable and curative therapies. The team’s mission is to provide safe, effective, and affordable medicines for diseases with unmet medical needs.